RNA-BASE GENE THERAPY OF PRIMARY MYOPATHIES: USE OF ANTISENSE RNAS FOR THE CORRECTION, AT THE POST-TRANSCRIPTIONAL LEVEL, OF MUTATED DYSTROPHIN PRE-MRNAS
- 2 Anni 1999/2001
- 103.291€ Totale Fondi
Descrizione non disponibile
Pubblicazioni Scientifiche
- 2002 PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AME
Chimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cells
